Drug | Indication |
---|---|
Ipilimumab | Melanoma |
Vemurafenib | Melanoma |
Taliglucerase alfa | Gaucher disease |
Ivacaftor | Cystic fibrosis |
Vismodegib | Basal cell carcinoma |
Dabrafenib mesylate | Melanoma |
Mipomersen sodium | Homozygous familial hypercholesterolemia |
Trametinib dimethyl sulfoxide | Melanoma |